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Mean NSAA changes in the subgroups amenable to skip exons 44, 45, 51 and 53 according to age.

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posted on 2021-06-25, 17:26 authored by Giorgia Coratti, Marika Pane, Claudia Brogna, Valeria Ricotti, Sonia Messina, Adele D’Amico, Claudio Bruno, Gianluca Vita, Angela Berardinelli, Elena Mazzone, Francesca Magri, Federica Ricci, Tiziana Mongini, Roberta Battini, Luca Bello, Elena Pegoraro, Giovanni Baranello, Stefano C. Previtali, Luisa Politano, Giacomo P. Comi, Valeria A. Sansone, Alice Donati, Jean Yves Hogrel, Volker Straub, Silvana De Lucia, Erik Niks, Laurent Servais, Imelda De Groot, Mary Chesshyre, Enrico Bertini, Nathalie Goemans, Francesco Muntoni, Eugenio Mercuri

Panel A: Study Cohort. Panel B: <7 years of age. Panel C: ≥7 years of age. ··· = amenable to skip 44, — = amenable to skip 45,––– = amenable to skip 51,––– = amenable to skip 53.

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